Dichloroacetate Missed Its Main Goal in Kids With Rare Energy Disorder PDCD, but Lowered Lactate
TL;DR: In a phase III trial of 34 children with a rare inherited energy disorder, the drug dichloroacetate did not improve parent-rated movement problems more than placebo over 4 months. It did lower a harmful blood acid, lactate, and was well tolerated. Key F…
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